The Foundation Fighting Blindness, the world’s leading organization committed to finding treatments and cures for blinding diseases, is committing at least $8.6 million for its Uni-Rare Study, a new natural history study, and will begin recruiting in December.
This study will help clinical researchers gain a better understanding of the course of retinal degeneration and vision loss for people with mutated genes that have not been well-characterized in the clinic.
The study will also help the IRD research and therapeutic development community:
1) identify more people for clinical trials of therapies,
2) inform design of clinical trials, and
3) identify therapeutic targets for more people.